HSPB8 Myopathy We’re still energized after an incredible few days at the World Orphan Drug Congress USA 2025 , held April 22–24 in Boston! This dynamic gathering brought together over 2,000 stakeholders across the…

New on the Cure HSPB8 blog!
We just got back from the World Orphan Drug Congress USA 2025, where we shared our story, our science, and our vision for a cure.
Read our recap here: 🔗 buff.ly/qJcfmJO

#WODCUSA #RareDisease #HSPB8 #CureHSPB8 #OrphanDrugDevelopment #HopeInScience